Patent Application Titled "Methods And Compositions For Treating Tecpr2-Associated Disease And Disorders With A Viral Vector" Published Online (USPTO 20240024512).
In: Gene Therapy Weekly, 2024-02-16, S. 3555-3555
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Zugriff:
The USPTO has published a patent application titled "Methods And Compositions For Treating Tecpr2-Associated Disease And Disorders With A Viral Vector." The application, filed by inventors from the University of Florida Research Foundation, outlines a gene therapy method for treating neuropathies caused by mutations in the TECPR2 gene. The invention involves using recombinant adeno-associated virus (rAAV) vectors to deliver a TECPR2-encoding nucleic acid to nervous system tissues, potentially offering a treatment option for severe neurodegenerative disorders like spastic paraplegia type 49 (SPG49) and hereditary sensory and autonomic neuropathy type IX (HSAN9). The patent application also discusses administration routes and potential symptom improvements associated with these disorders. [Extracted from the article]
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Patent Application Titled "Methods And Compositions For Treating Tecpr2-Associated Disease And Disorders With A Viral Vector" Published Online (USPTO 20240024512).
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Zeitschrift: | Gene Therapy Weekly, 2024-02-16, S. 3555-3555 |
Veröffentlichung: | 2024 |
Medientyp: | serialPeriodical |
ISSN: | 1078-2842 (print) |
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