Researchers Submit Patent Application, "Genome Editing Compositions And Methods For Treatment Of Wilson'S Disease", for Approval (USPTO 20240167026).
In: Gene Therapy Weekly, 2024-06-11, S. 4818-4818
serialPeriodical
Zugriff:
A patent application has been submitted for a genome editing method to treat Wilson's disease, a genetic disorder caused by mutations in the ATP7B gene. The current treatments for Wilson's disease involve medication or liver transplantation, but gene therapy could offer a more effective solution. The patent application describes a prime editing method using a guide RNA that can correct mutations in the ATP7B gene. The patent document provides specific sequences and components for the guide RNA, which could be used in gene therapy for Wilson's disease. [Extracted from the article]
Copyright of Gene Therapy Weekly is the property of NewsRx and its content may not be copied or emailed to multiple sites or posted to a listserv without the copyright holder's express written permission. However, users may print, download, or email articles for individual use. This abstract may be abridged. No warranty is given about the accuracy of the copy. Users should refer to the original published version of the material for the full abstract. (Copyright applies to all Abstracts.)
Titel: |
Researchers Submit Patent Application, "Genome Editing Compositions And Methods For Treatment Of Wilson'S Disease", for Approval (USPTO 20240167026).
|
---|---|
Zeitschrift: | Gene Therapy Weekly, 2024-06-11, S. 4818-4818 |
Veröffentlichung: | 2024 |
Medientyp: | serialPeriodical |
ISSN: | 1078-2842 (print) |
Schlagwort: |
|
Sonstiges: |
|